National Niemann-Pick Disease Foundation, Inc. - October is

Families plead with FDA for drug to treat Niemann-Pick Disease Type C

Improved systemic AAV gene therapy with a neurotrophic capsid in Niemann–Pick disease type C1 mice

National Niemann-Pick Disease Foundation, Inc. - October is Niemann-Pick Awareness Month! Support NNPDF, every penny helps our Niemann-Pick families, programs, and research. Make a gift and learn more about Niemann-Pick disease at

Reflecting on the past and looking forward with hope during Niemann-Pick Disease Awareness Month

Niemann–Pick disease - Wikipedia

Prevalence of dysphagia in Niemann-Pick disease type C (NP-C) and other

Zevra Therapeutics Celebrates and Supports Global Niemann-Pick Disease Awareness Day on October 19th and Niemann-Pick Disease Awareness Month Throughout October

And Life Goes OnAn Angel and a Rainbow: October 2017

National Niemann-Pick Disease Foundation, Inc. - October is Global Niemann-Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to the NNPDF go to www.nnpdf.org. #niemannpick #ASMD #

September 2023 Newsletter – NNPDF

Blog – NNPDF